Clinical trials
Active, not recruiting Mucopolysaccharidosis II trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
9 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2014 | 1 |
| 2017 | 1 |
| 2018 | 2 |
| 2020 | 1 |
| 2021 | 1 |
| 2022 | 2 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Active, not recruiting | 9 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| REGENXBIO Inc. | 3 |
| Denali Therapeutics Inc. | 2 |
| JCR Pharmaceuticals Co., Ltd. | 1 |
| Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center | 1 |
| Masonic Cancer Center, University of Minnesota | 1 |
| RTI International | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis II | 9 |
| Sudden Infant Death | 5 |
| Mucopolysaccharidosis I | 3 |
| Mucopolysaccharidosis VI | 3 |
| Leukodystrophy, Globoid Cell | 2 |
| Leukodystrophy, Metachromatic | 2 |
| Mucopolysaccharidosis VII | 2 |
| Peroxisomal Disorders | 2 |
| Anemia, Sickle Cell | 1 |
| Angelman Syndrome | 1 |
Trials
Showing 1 to 9 of 9. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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