Clinical trials
Completed Mucopolysaccharidosis II trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
24 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2004 | 1 |
| 2005 | 2 |
| 2008 | 2 |
| 2009 | 5 |
| 2010 | 1 |
| 2012 | 1 |
| 2013 | 1 |
| 2014 | 2 |
| 2015 | 4 |
| 2017 | 1 |
| 2019 | 1 |
| 2021 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 24 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Shire | 12 |
| REGENXBIO Inc. | 2 |
| ArmaGen, Inc | 1 |
| Denali Therapeutics Inc. | 1 |
| Duke University | 1 |
| Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | 1 |
| Joanne Kurtzberg, MD | 1 |
| Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center | 1 |
| Masonic Cancer Center, University of Minnesota | 1 |
| Takeda | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis II | 24 |
| Sudden Infant Death | 12 |
| Lysosomal Storage Diseases | 8 |
| Mucopolysaccharidoses | 7 |
| Mucopolysaccharidosis I | 6 |
| Mucopolysaccharidosis VI | 4 |
| Metabolism, Inborn Errors | 3 |
| Leukodystrophy, Globoid Cell | 2 |
| Mucopolysaccharidosis III | 2 |
| Mucopolysaccharidosis VII | 2 |
Trials
Showing 1 to 24 of 24. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.