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Clinical trials

Completed Observational Mucopolysaccharidosis II trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Mucopolysaccharidosis II Phase: Observational Status: Completed Clear all

14 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20051
20081
20093
20122
20131
20172
20181
20191
20201
20221

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed14

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Shire6
Centre Hospitalier Universitaire de Liege1
Denali Therapeutics Inc.1
GlaxoSmithKline1
Manchester University NHS Foundation Trust1
REGENXBIO Inc.1
University Hospital Heidelberg1
University of Chicago1
University of Minnesota1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Mucopolysaccharidosis II14
Sudden Infant Death5
Mucopolysaccharidosis I4
Mucopolysaccharidoses3
Mucopolysaccharidosis VI3
Lysosomal Storage Diseases2
Mucopolysaccharidosis III2
Mucopolysaccharidosis IV2
Mucopolysaccharidosis VII2
Adrenal Hyperplasia, Congenital1

Trials

Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.

Recently changed trials

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