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Clinical trials

Observational beta-Thalassemia trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: beta-Thalassemia Phase: Observational Country / region: United States Clear all

16 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20001
20041
20071
20111
20131
20141
20181
20192
20201
20212
20221
20243

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed6
Recruiting5
Active, not recruiting2
Unknown status2
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Sanguine Biosciences2
Ann & Robert H Lurie Children's Hospital of Chicago1
Carelon Research1
Celgene Corporation1
Columbia University1
Cyprus Institute of Neurology and Genetics1
Dana-Farber Cancer Institute1
Editas Medicine, Inc.1
Genetix Biotherapeutics Inc.1
National Institute of Allergy and Infectious Diseases (NIAID)1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
beta-Thalassemia16
Anemia, Sickle Cell11
Cystic Fibrosis4
Crohn Disease3
Diabetes Mellitus3
Iron Overload3
Muscular Dystrophy, Duchenne3
Alopecia Areata2
Alzheimer Disease2
Amyloidosis2

Trials

Showing 1 to 16 of 16. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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