Clinical trials
Phase 1/2 beta-Thalassemia trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
11 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2004 | 1 |
| 2008 | 1 |
| 2011 | 1 |
| 2018 | 2 |
| 2020 | 1 |
| 2022 | 2 |
| 2025 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Active, not recruiting | 3 |
| Completed | 3 |
| Recruiting | 3 |
| Enrolling by invitation | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Heart, Lung, and Blood Institute (NHLBI) | 3 |
| Children's Hospital of Philadelphia | 1 |
| Editas Medicine, Inc. | 1 |
| Genzyme, a Sanofi Company | 1 |
| Northwell Health | 1 |
| Paul Szabolcs | 1 |
| Phoenicia BioScience | 1 |
| Sangamo Therapeutics | 1 |
| Talaris Therapeutics Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| beta-Thalassemia | 11 |
| Anemia, Sickle Cell | 7 |
| Anemia, Diamond-Blackfan | 2 |
| Thalassemia | 2 |
| Anemia | 1 |
| Anemia, Hemolytic, Congenital | 1 |
| Bone Marrow Failure Disorders | 1 |
| Hemoglobinopathies | 1 |
| alpha-Thalassemia | 1 |
Trials
Showing 1 to 11 of 11. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.