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Clinical trials

alpha 1-Antitrypsin Deficiency trials in the United Kingdom

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: alpha 1-Antitrypsin Deficiency Country / region: United Kingdom Clear all

26 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20031
20061
20091
20152
20181
20193
20202
20211
20221
20235
20245
20251
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed9
Recruiting7
Terminated6
Active, not recruiting3
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Takeda4
Arrowhead Pharmaceuticals2
Grifols Therapeutics LLC2
Kamada, Ltd.2
Sanofi2
Vertex Pharmaceuticals Incorporated2
Wave Life Sciences USA, Inc.2
AIRNA Corporation1
Alnylam Pharmaceuticals1
Beam Therapeutics Inc.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
alpha 1-Antitrypsin Deficiency26
Emphysema5
Lung Diseases2
Pulmonary Disease, Chronic Obstructive2
Congenital Abnormalities1
Genetic Diseases, Inborn1
Infant, Newborn, Diseases1
Liver Diseases1
Pathologic Processes1
Pathological Conditions, Signs and Symptoms1

Trials

Showing 1 to 25 of 26. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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