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Clinical trials

Terminated alpha 1-Antitrypsin Deficiency trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: alpha 1-Antitrypsin Deficiency Status: Terminated Country / region: United States Clear all

12 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20102
20121
20141
20151
20161
20181
20201
20211
20231

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Terminated12

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Baxalta now part of Shire2
Vertex Pharmaceuticals Incorporated2
Columbia University1
Dicerna Pharmaceuticals, Inc., a Novo Nordisk company1
Grifols Therapeutics LLC1
National Center for Research Resources (NCRR)1
National Institute of Allergy and Infectious Diseases (NIAID)1
University of Florida1
University of North Carolina, Chapel Hill1
Washington University School of Medicine1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
alpha 1-Antitrypsin Deficiency12
Pulmonary Disease, Chronic Obstructive4
Diabetes Mellitus, Type 12
Bronchiectasis1
Cough1
Cystic Fibrosis1
Diabetes Mellitus1
Emphysema1
Genetic Diseases, Inborn1
Hypertension, Pulmonary1

Trials

Showing 1 to 12 of 12. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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