Clinical trials
Phase 1 alpha 1-Antitrypsin Deficiency trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
19 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2004 | 1 |
| 2005 | 1 |
| 2006 | 1 |
| 2010 | 2 |
| 2015 | 2 |
| 2018 | 1 |
| 2019 | 2 |
| 2020 | 1 |
| 2022 | 1 |
| 2023 | 2 |
| 2024 | 1 |
| 2025 | 3 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 10 |
| Terminated | 4 |
| Recruiting | 3 |
| Active, not recruiting | 2 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Arrowhead Pharmaceuticals | 2 |
| University of Massachusetts, Worcester | 2 |
| Vertex Pharmaceuticals Incorporated | 2 |
| AIRNA Corporation | 1 |
| Alnylam Pharmaceuticals | 1 |
| Baxalta now part of Shire | 1 |
| BioMarin Pharmaceutical | 1 |
| Dicerna Pharmaceuticals, Inc., a Novo Nordisk company | 1 |
| Inhibrx Biosciences, Inc | 1 |
| Krystal Biotech, Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| alpha 1-Antitrypsin Deficiency | 19 |
| Diabetes Mellitus | 2 |
| Diabetes Mellitus, Type 1 | 2 |
| Emphysema | 2 |
| Congenital Abnormalities | 1 |
| Genetic Diseases, Inborn | 1 |
| Infant, Newborn, Diseases | 1 |
| Liver Diseases | 1 |
| Lung Diseases | 1 |
| Pathologic Processes | 1 |
Trials
Showing 1 to 19 of 19. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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