Clinical trials
Phase 1/2 alpha 1-Antitrypsin Deficiency trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
14 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2004 | 1 |
| 2014 | 1 |
| 2016 | 2 |
| 2017 | 2 |
| 2021 | 1 |
| 2024 | 3 |
| 2025 | 1 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 7 |
| Recruiting | 2 |
| Not yet recruiting | 1 |
| Active, not recruiting | 1 |
| Terminated | 1 |
| Unknown status | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Grifols Therapeutics LLC | 3 |
| Baxalta now part of Shire | 2 |
| Adverum Biotechnologies, Inc. | 1 |
| Beam Therapeutics Inc. | 1 |
| CRISPR Therapeutics | 1 |
| Intellia Therapeutics | 1 |
| Korro Bio, Inc. | 1 |
| Medical University of South Carolina | 1 |
| Soroka University Medical Center | 1 |
| Tessera Therapeutics, Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| alpha 1-Antitrypsin Deficiency | 14 |
| Lung Diseases | 3 |
| Emphysema | 2 |
| Pulmonary Disease, Chronic Obstructive | 2 |
| Digestive System Diseases | 1 |
| Genetic Diseases, Inborn | 1 |
| Inflammation | 1 |
| Liver Diseases | 1 |
| Lung Diseases, Obstructive | 1 |
| Pancreatitis, Chronic | 1 |
Trials
Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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