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Clinical trials

Completed Phase 1 alpha 1-Antitrypsin Deficiency trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: alpha 1-Antitrypsin Deficiency Phase: Phase 1 Status: Completed Clear all

10 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20041
20051
20061
20101
20181
20192
20221
20232

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed10

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
University of Massachusetts, Worcester2
Vertex Pharmaceuticals Incorporated2
Arrowhead Pharmaceuticals1
Baxalta now part of Shire1
Dicerna Pharmaceuticals, Inc., a Novo Nordisk company1
Inhibrx Biosciences, Inc1
University of Colorado, Denver1
Wave Life Sciences USA, Inc.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
alpha 1-Antitrypsin Deficiency10
Diabetes Mellitus1
Diabetes Mellitus, Type 11

Trials

Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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