Clinical trials
Heredodegenerative Disorders, Nervous System trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
21 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2009 | 1 |
| 2011 | 2 |
| 2012 | 1 |
| 2017 | 1 |
| 2019 | 1 |
| 2020 | 2 |
| 2021 | 2 |
| 2022 | 3 |
| 2023 | 1 |
| 2024 | 2 |
| 2025 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
| Recruiting | 4 |
| Terminated | 2 |
| Active, not recruiting | 2 |
| Withdrawn | 1 |
| Enrolling by invitation | 1 |
| Not yet recruiting | 1 |
| No longer available | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| PepGen Inc | 2 |
| Siena Biotech S.p.A. | 2 |
| State University of New York at Buffalo | 2 |
| SwanBio Therapeutics, Inc. | 2 |
| Vertex Pharmaceuticals Incorporated | 2 |
| AO GENERIUM | 1 |
| Alnylam Pharmaceuticals | 1 |
| Avidity Biosciences, Inc. | 1 |
| Intellia Therapeutics | 1 |
| National Cancer Institute (NCI) | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Heredodegenerative Disorders, Nervous System | 21 |
| Nervous System Diseases | 12 |
| Genetic Diseases, Inborn | 11 |
| Neurodegenerative Diseases | 10 |
| Neuromuscular Diseases | 7 |
| Metabolic Diseases | 5 |
| Muscular Diseases | 5 |
| Muscular Disorders, Atrophic | 5 |
| Musculoskeletal Diseases | 5 |
| Myotonic Disorders | 5 |
Trials
Showing 1 to 21 of 21. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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