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Clinical trials

Phase 1/2 Heredodegenerative Disorders, Nervous System trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Heredodegenerative Disorders, Nervous System Phase: Phase 1/2 Country / region: United States Clear all

2 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20221
20241

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Active, not recruiting1
Terminated1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
SwanBio Therapeutics, Inc.1
Vertex Pharmaceuticals Incorporated1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Heredodegenerative Disorders, Nervous System2
Adrenal Insufficiency1
Adrenoleukodystrophy1
Brain Diseases, Metabolic1
Brain Diseases, Metabolic, Inborn1
Demyelinating Diseases1
Genetic Diseases, Inborn1
Hereditary Central Nervous System Demyelinating Diseases1
Leukoencephalopathies1
Metabolic Diseases1

Trials

Showing 1 to 2 of 2. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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