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Clinical trials

Phase 3 Muscular Dystrophy, Duchenne trials in Australia

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophy, Duchenne Phase: Phase 3 Country / region: Australia Clear all

18 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20081
20101
20111
20121
20131
20141
20161
20171
20181
20191
20203
20212
20231
20251
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed8
Terminated5
Active, not recruiting2
Recruiting2
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
PTC Therapeutics4
Catabasis Pharmaceuticals2
Kyntra Bio2
NS Pharma, Inc.2
Novartis Pharmaceuticals2
Sarepta Therapeutics, Inc.2
Avidity Biosciences, Inc.1
GlaxoSmithKline1
Pfizer1
Solid Biosciences Inc.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophy, Duchenne18
Muscular Dystrophies8
Musculoskeletal Diseases7
Neuromuscular Diseases7
Genetic Diseases, Inborn5
Muscular Diseases5
Muscular Disorders, Atrophic5
Nervous System Diseases5
Genetic Diseases, X-Linked4
Osteoporosis2

Trials

Showing 1 to 18 of 18. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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