Clinical trials
Phase 3 Muscular Dystrophy, Duchenne trials in Canada
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
25 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 1 |
| 2010 | 3 |
| 2011 | 1 |
| 2012 | 1 |
| 2013 | 4 |
| 2014 | 1 |
| 2016 | 1 |
| 2017 | 2 |
| 2018 | 2 |
| 2019 | 1 |
| 2020 | 3 |
| 2021 | 2 |
| 2023 | 1 |
| 2024 | 1 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 11 |
| Terminated | 9 |
| Active, not recruiting | 2 |
| Recruiting | 2 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| PTC Therapeutics | 5 |
| Sarepta Therapeutics, Inc. | 3 |
| Catabasis Pharmaceuticals | 2 |
| GlaxoSmithKline | 2 |
| Italfarmaco | 2 |
| Kyntra Bio | 2 |
| NS Pharma, Inc. | 2 |
| Novartis Pharmaceuticals | 2 |
| BioMarin Pharmaceutical | 1 |
| Eli Lilly and Company | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Muscular Dystrophy, Duchenne | 25 |
| Muscular Dystrophies | 10 |
| Neuromuscular Diseases | 7 |
| Musculoskeletal Diseases | 6 |
| Genetic Diseases, Inborn | 4 |
| Genetic Diseases, X-Linked | 4 |
| Muscular Diseases | 4 |
| Muscular Disorders, Atrophic | 4 |
| Nervous System Diseases | 4 |
| Osteoporosis | 2 |
Trials
Showing 1 to 25 of 25. Each trial links to its page on Pharma Observatory.
Recently changed trials
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