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Clinical trials

Muscular Dystrophy, Duchenne trials in the United Kingdom

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophy, Duchenne Country / region: United Kingdom Clear all

84 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20071
20082
20092
20103
20112
20123
20136
20142
20154
20168
20175
20186
20195
20204
20216
20224
20236
20245
20255
20264

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed34
Terminated20
Active, not recruiting11
Recruiting9
Enrolling by invitation4
Unknown status3
Not yet recruiting2
No longer available1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Sarepta Therapeutics, Inc.11
PTC Therapeutics7
BioMarin Pharmaceutical5
Italfarmaco4
ReveraGen BioPharma, Inc.4
Wave Life Sciences USA, Inc.4
Entrada Therapeutics, Inc.3
Pfizer3
Santhera Pharmaceuticals3
Summit Therapeutics3

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophy, Duchenne84
Muscular Dystrophies14
Neuromuscular Diseases8
Musculoskeletal Diseases6
Genetic Diseases, Inborn4
Muscular Diseases4
Muscular Disorders, Atrophic4
Nervous System Diseases4
Genetic Diseases, X-Linked3
Osteoporosis2

Trials

Showing 1 to 25 of 84. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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