Clinical trials
Muscular Dystrophy, Duchenne trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
231 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 2 |
| 2001 | 1 |
| 2002 | 3 |
| 2004 | 2 |
| 2005 | 4 |
| 2006 | 2 |
| 2007 | 3 |
| 2008 | 2 |
| 2009 | 5 |
| 2010 | 12 |
| 2011 | 6 |
| 2012 | 12 |
| 2013 | 13 |
| 2014 | 11 |
| 2015 | 11 |
| 2016 | 15 |
| 2017 | 11 |
| 2018 | 21 |
| 2019 | 10 |
| 2020 | 14 |
| 2021 | 11 |
| 2022 | 15 |
| 2023 | 6 |
| 2024 | 15 |
| 2025 | 10 |
| 2026 | 8 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 117 |
| Terminated | 39 |
| Recruiting | 28 |
| Active, not recruiting | 25 |
| Enrolling by invitation | 8 |
| Unknown status | 5 |
| Withdrawn | 3 |
| No longer available | 2 |
| Available | 2 |
| Not yet recruiting | 1 |
| Approved for marketing | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Sarepta Therapeutics, Inc. | 23 |
| Cooperative International Neuromuscular Research Group | 15 |
| PTC Therapeutics | 15 |
| University of Florida | 9 |
| Cedars-Sinai Medical Center | 7 |
| NS Pharma, Inc. | 7 |
| Pfizer | 7 |
| Edgewise Therapeutics, Inc. | 6 |
| Nationwide Children's Hospital | 6 |
| Capricor Inc. | 5 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Muscular Dystrophy, Duchenne | 231 |
| Muscular Dystrophies | 56 |
| Neuromuscular Diseases | 20 |
| Muscular Diseases | 11 |
| Cardiomyopathies | 9 |
| Genetic Diseases, Inborn | 9 |
| Muscular Dystrophies, Limb-Girdle | 9 |
| Genetic Diseases, X-Linked | 8 |
| Musculoskeletal Diseases | 8 |
| Nervous System Diseases | 8 |
Trials
Showing 1 to 25 of 231. Each trial links to its page on Pharma Observatory.
131 more trials match. See them on Pharma Observatory
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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