Clinical trials
Phase 1 Muscular Dystrophy, Duchenne trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
32 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2006 | 1 |
| 2007 | 1 |
| 2009 | 1 |
| 2010 | 1 |
| 2011 | 1 |
| 2012 | 3 |
| 2013 | 1 |
| 2014 | 3 |
| 2015 | 3 |
| 2017 | 1 |
| 2018 | 4 |
| 2020 | 3 |
| 2021 | 2 |
| 2022 | 1 |
| 2024 | 1 |
| 2025 | 3 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 23 |
| Terminated | 5 |
| Recruiting | 3 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Cedars-Sinai Medical Center | 5 |
| Sarepta Therapeutics, Inc. | 4 |
| Nationwide Children's Hospital | 3 |
| Edgewise Therapeutics, Inc. | 2 |
| PTC Therapeutics | 2 |
| Allergy and Asthma Consultants, Wichita, Kansas | 1 |
| Astellas Pharma Inc | 1 |
| Cure Rare Disease, Inc | 1 |
| Epirium Bio Inc. | 1 |
| GlaxoSmithKline | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Muscular Dystrophy, Duchenne | 32 |
| Muscular Dystrophies | 10 |
| Cardiomyopathies | 1 |
| Heart Failure | 1 |
| Muscular Diseases | 1 |
| Muscular Dystrophies, Limb-Girdle | 1 |
| Myositis, Inclusion Body | 1 |
Trials
Showing 1 to 25 of 32. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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