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Clinical trials

Phase 1/2 Muscular Dystrophy, Duchenne trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophy, Duchenne Phase: Phase 1/2 Country / region: United States Clear all

25 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20021
20052
20101
20132
20152
20163
20172
20183
20191
20201
20211
20222
20242
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed14
Active, not recruiting4
Recruiting2
Terminated2
Withdrawn1
Unknown status1
Not yet recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Sarepta Therapeutics, Inc.4
Cooperative International Neuromuscular Research Group2
Craig McDonald, MD2
Kevin Flanigan2
Solid Biosciences Inc.2
Avidity Biosciences, Inc.1
Catabasis Pharmaceuticals1
Children's Hospital Medical Center, Cincinnati1
Children's National Research Institute1
Dyne Therapeutics1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophy, Duchenne25
Muscular Dystrophies4
Neuromuscular Diseases2
Cardiomyopathies1
Muscular Diseases1
Muscular Dystrophies, Limb-Girdle1
Muscular Dystrophy, Facioscapulohumeral1
Musculoskeletal Diseases1
Nervous System Diseases1
Obesity1

Trials

Showing 1 to 25 of 25. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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