Clinical trials
Active, not recruiting Muscular Dystrophy, Duchenne trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
25 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2012 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2018 | 1 |
| 2020 | 3 |
| 2021 | 3 |
| 2022 | 5 |
| 2023 | 2 |
| 2024 | 5 |
| 2025 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Active, not recruiting | 25 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| NS Pharma, Inc. | 3 |
| Capricor Inc. | 2 |
| Edgewise Therapeutics, Inc. | 2 |
| REGENXBIO Inc. | 2 |
| Sarepta Therapeutics, Inc. | 2 |
| Avidity Biosciences, Inc. | 1 |
| Children's Hospital Medical Center, Cincinnati | 1 |
| Dyne Therapeutics | 1 |
| Hoffmann-La Roche | 1 |
| Insmed Gene Therapy LLC | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Muscular Dystrophy, Duchenne | 25 |
| Muscular Dystrophies | 4 |
| Neuromuscular Diseases | 2 |
| Anemia, Sickle Cell | 1 |
| Angelman Syndrome | 1 |
| Aortic Stenosis, Supravalvular | 1 |
| Argininosuccinic Aciduria | 1 |
| Barth Syndrome | 1 |
| Biotinidase Deficiency | 1 |
| Canavan Disease | 1 |
Trials
Showing 1 to 25 of 25. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
Go deeper on Pharma Observatory
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