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Clinical trials

Approved for marketing Expanded access Muscular Dystrophy, Duchenne trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophy, Duchenne Phase: Expanded access Status: Approved for marketing Clear all

2 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

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Trials by status
CategoryTrials
Approved for marketing2

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
NS Pharma, Inc.1
PTC Therapeutics1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophy, Duchenne2
Genetic Diseases, Inborn1
Genetic Diseases, X-Linked1
Muscular Diseases1
Muscular Disorders, Atrophic1
Muscular Dystrophies1
Musculoskeletal Diseases1
Nervous System Diseases1
Neuromuscular Diseases1

Trials

Showing 1 to 2 of 2. Each trial links to its page on Pharma Observatory.

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