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Clinical trials

Completed Phase 1/2 Muscular Dystrophy, Duchenne trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophy, Duchenne Phase: Phase 1/2 Status: Completed Clear all

20 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20021
20052
20071
20092
20101
20132
20153
20162
20171
20182
20191
20201
20221

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed20

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Sarepta Therapeutics, Inc.4
Cooperative International Neuromuscular Research Group2
Craig McDonald, MD2
Avidity Biosciences, Inc.1
BioMarin Pharmaceutical1
Catabasis Pharmaceuticals1
Children's Hospital Medical Center, Cincinnati1
Daiichi Sankyo Co., Ltd.1
Imperial College London1
Italfarmaco1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophy, Duchenne20
Muscular Dystrophies3
Neuromuscular Diseases2
Cardiomyopathies1
Muscular Diseases1
Muscular Dystrophies, Limb-Girdle1
Muscular Dystrophy, Facioscapulohumeral1
Musculoskeletal Diseases1
Nervous System Diseases1
Rare Diseases1

Trials

Showing 1 to 20 of 20. Each trial links to its page on Pharma Observatory.

Recently changed trials

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