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Clinical trials

Phase 3 Muscular Dystrophy, Duchenne trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophy, Duchenne Phase: Phase 3 Clear all

49 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20041
20071
20081
20092
20103
20111
20122
20135
20143
20151
20162
20172
20185
20191
20205
20214
20221
20233
20241
20251
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed22
Terminated14
Recruiting4
Active, not recruiting4
Unknown status2
Withdrawn2
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Sarepta Therapeutics, Inc.7
PTC Therapeutics6
GlaxoSmithKline3
Santhera Pharmaceuticals3
Assistance Publique - Hôpitaux de Paris2
Catabasis Pharmaceuticals2
Cooperative International Neuromuscular Research Group2
Italfarmaco2
Kyntra Bio2
NS Pharma, Inc.2

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophy, Duchenne49
Muscular Dystrophies18
Neuromuscular Diseases11
Genetic Diseases, Inborn8
Musculoskeletal Diseases7
Genetic Diseases, X-Linked6
Muscular Diseases6
Muscular Disorders, Atrophic6
Nervous System Diseases6
Myotonic Dystrophy2

Trials

Showing 1 to 25 of 49. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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