Clinical trials
Amyloidosis, Familial trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
28 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2006 | 1 |
| 2012 | 1 |
| 2013 | 2 |
| 2014 | 1 |
| 2016 | 1 |
| 2019 | 4 |
| 2020 | 3 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 4 |
| 2024 | 4 |
| 2025 | 1 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
| Recruiting | 8 |
| Withdrawn | 3 |
| Active, not recruiting | 3 |
| Not yet recruiting | 2 |
| Approved for marketing | 2 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Alnylam Pharmaceuticals | 10 |
| Eidos Therapeutics, a BridgeBio company | 3 |
| Boston University | 2 |
| Intellia Therapeutics | 2 |
| AstraZeneca | 1 |
| Brigham and Women's Hospital | 1 |
| Centre Hospitalier Universitaire de Nice | 1 |
| Fondazione Policlinico Universitario Agostino Gemelli IRCCS | 1 |
| Hospital de Alta Complejidad en Red | 1 |
| Ionis Pharmaceuticals, Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amyloidosis, Familial | 28 |
| Amyloidosis | 17 |
| Amyloid Neuropathies, Familial | 16 |
| Amyloid Neuropathies | 8 |
| Polyneuropathies | 8 |
| Alzheimer Disease | 5 |
| Cardiomyopathies | 4 |
| Peripheral Nervous System Diseases | 3 |
| Genetic Diseases, Inborn | 2 |
| Heredodegenerative Disorders, Nervous System | 2 |
Trials
Showing 1 to 25 of 28. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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