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Clinical trials

Amyloid Neuropathies, Familial trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Amyloid Neuropathies, Familial Country / region: United States Clear all

58 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20071
20136
20142
20151
20162
20172
20182
20194
20204
20213
20224
20236
20247
20257
20266

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed25
Recruiting17
Terminated4
Active, not recruiting3
Enrolling by invitation3
Not yet recruiting2
Unknown status2
Withdrawn2

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Eidos Therapeutics, a BridgeBio company7
Alnylam Pharmaceuticals6
Brigham and Women's Hospital6
Mayo Clinic3
Pfizer3
Cedars-Sinai Medical Center2
Ionis Pharmaceuticals, Inc.2
The Cleveland Clinic2
University of Pennsylvania2
University of Texas Southwestern Medical Center2

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Amyloid Neuropathies, Familial58
Amyloidosis29
Alzheimer Disease12
Amyloidosis, Familial10
Cardiomyopathies8
Polyneuropathies8
Heart Failure6
Amyloid Neuropathies5
Immunoglobulin Light-chain Amyloidosis4
Disease3

Trials

Showing 1 to 25 of 58. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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