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Clinical trials

Completed Genetic Diseases, Inborn trials in Belgium

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Genetic Diseases, Inborn Status: Completed Country / region: Belgium Clear all

14 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20091
20101
20111
20131
20141
20151
20161
20174
20182

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed14

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Eloxx Pharmaceuticals, Inc.2
Alexion Pharmaceuticals, Inc.1
BioMarin Pharmaceutical1
Novartis Pharmaceuticals1
Novo Nordisk A/S1
PTC Therapeutics1
Pfizer1
Quince Therapeutics S.p.A.1
Swedish Orphan Biovitrum1
University Hospital, Ghent1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Genetic Diseases, Inborn14
Blood Coagulation Disorders2
Coagulation Protein Disorders2
Cystic Fibrosis2
Hematologic Diseases2
Hemophilia A2
Hemorrhagic Disorders2
Infant, Newborn, Diseases2
Lung Diseases2
Nervous System Diseases2

Trials

Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.

Recently changed trials

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