Clinical trials
Observational Genetic Diseases, Inborn trials in Brazil
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
4 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2015 | 1 |
| 2022 | 1 |
| 2023 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 1 |
| Enrolling by invitation | 1 |
| Recruiting | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Azafaros B.V. | 1 |
| BioMarin Pharmaceutical | 1 |
| Friedreich's Ataxia Research Alliance | 1 |
| Shire | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 4 |
| Lysosomal Storage Diseases | 2 |
| Nervous System Diseases | 2 |
| Ataxia | 1 |
| Blood Coagulation Disorders | 1 |
| Blood Coagulation Disorders, Inherited | 1 |
| Brain Diseases | 1 |
| Brain Diseases, Metabolic, Inborn | 1 |
| Central Nervous System Diseases | 1 |
| Coagulation Protein Disorders | 1 |
Trials
Showing 1 to 4 of 4. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.