Clinical trials
Observational Genetic Diseases, Inborn trials in Canada
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
14 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2007 | 1 |
| 2012 | 1 |
| 2015 | 1 |
| 2017 | 1 |
| 2019 | 4 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 1 |
| 2024 | 2 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 5 |
| Recruiting | 4 |
| Terminated | 2 |
| Enrolling by invitation | 1 |
| Suspended | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| QED Therapeutics, a BridgeBio company | 2 |
| Arbor Research Collaborative for Health | 1 |
| CSL Behring | 1 |
| Editas Medicine, Inc. | 1 |
| Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | 1 |
| Friedreich's Ataxia Research Alliance | 1 |
| HemoShear Therapeutics | 1 |
| REGENXBIO Inc. | 1 |
| Shire | 1 |
| Spark Therapeutics, Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 14 |
| Metabolic Diseases | 4 |
| Metabolism, Inborn Errors | 3 |
| Musculoskeletal Diseases | 3 |
| Bone Diseases | 2 |
| Brain Diseases | 2 |
| Brain Diseases, Metabolic, Inborn | 2 |
| Central Nervous System Diseases | 2 |
| Dwarfism | 2 |
| Hematologic Diseases | 2 |
Trials
Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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