Clinical trials
Phase 1/2 Genetic Diseases, Inborn trials in Canada
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
10 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2016 | 1 |
| 2017 | 1 |
| 2021 | 4 |
| 2022 | 2 |
| 2024 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 4 |
| Active, not recruiting | 3 |
| Terminated | 2 |
| Completed | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| ModernaTX, Inc. | 5 |
| CHU de Quebec-Universite Laval | 1 |
| Editas Medicine, Inc. | 1 |
| REGENXBIO Inc. | 1 |
| Spark Therapeutics, Inc. | 1 |
| Vertex Pharmaceuticals Incorporated | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 10 |
| Metabolism, Inborn Errors | 4 |
| Metabolic Diseases | 3 |
| Acid-Base Imbalance | 2 |
| Acidosis | 2 |
| Amino Acid Metabolism, Inborn Errors | 2 |
| Hematologic Diseases | 2 |
| Propionic Acidemia | 2 |
| Anemia | 1 |
| Anemia, Hemolytic | 1 |
Trials
Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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