Clinical trials
Recruiting Genetic Diseases, Inborn trials in Canada
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2021 | 2 |
| 2022 | 2 |
| 2023 | 1 |
| 2024 | 1 |
| 2025 | 3 |
| 2026 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 12 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| ModernaTX, Inc. | 3 |
| BioMarin Pharmaceutical | 1 |
| Biossil Inc. | 1 |
| CHU de Quebec-Universite Laval | 1 |
| CSL Behring | 1 |
| Friedreich's Ataxia Research Alliance | 1 |
| PepGen Inc | 1 |
| QED Therapeutics, a BridgeBio company | 1 |
| The Hospital for Sick Children | 1 |
| University of Calgary | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 12 |
| Metabolism, Inborn Errors | 3 |
| Musculoskeletal Diseases | 3 |
| Acid-Base Imbalance | 2 |
| Acidosis | 2 |
| Amino Acid Metabolism, Inborn Errors | 2 |
| Bone Diseases | 2 |
| Metabolic Diseases | 2 |
| Osteochondrodysplasias | 2 |
| Propionic Acidemia | 2 |
Trials
Showing 1 to 12 of 12. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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