Clinical trials
Genetic Diseases, Inborn trials in Czechia
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2006 | 1 |
| 2009 | 1 |
| 2013 | 1 |
| 2014 | 1 |
| 2018 | 1 |
| 2019 | 1 |
| 2022 | 2 |
| 2023 | 1 |
| 2024 | 1 |
| 2025 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 6 |
| Recruiting | 5 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| PTC Therapeutics | 2 |
| Friedreich's Ataxia Research Alliance | 1 |
| Imagine Institute | 1 |
| Institute of Health Information and Statistics of the Czech Republic | 1 |
| Lipidica, a.s. | 1 |
| Masaryk Memorial Cancer Institute | 1 |
| NewAmsterdam Pharma | 1 |
| Novo Nordisk A/S | 1 |
| Pfizer | 1 |
| Swedish Orphan Biovitrum | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 12 |
| Nervous System Diseases | 3 |
| Genetic Diseases, X-Linked | 2 |
| Immune System Diseases | 2 |
| Muscular Diseases | 2 |
| Muscular Disorders, Atrophic | 2 |
| Muscular Dystrophies | 2 |
| Muscular Dystrophy, Duchenne | 2 |
| Musculoskeletal Diseases | 2 |
| Neuromuscular Diseases | 2 |
Trials
Showing 1 to 12 of 12. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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