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Clinical trials

Observational Genetic Diseases, Inborn trials in Czechia

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Genetic Diseases, Inborn Phase: Observational Country / region: Czechia Clear all

5 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20191
20231
20252

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting3
Completed2

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Friedreich's Ataxia Research Alliance1
Imagine Institute1
Institute of Health Information and Statistics of the Czech Republic1
Novo Nordisk A/S1
Swedish Orphan Biovitrum1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Genetic Diseases, Inborn5
Ataxia1
Autoimmune Diseases1
Blood Coagulation Disorders1
Coagulation Protein Disorders1
Congenital Abnormalities1
Dwarfism, Pituitary1
Fetal Growth Retardation1
Friedreich Ataxia1
Hematologic Diseases1

Trials

Showing 1 to 5 of 5. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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