Skip to content

Clinical trials

Completed Genetic Diseases, Inborn trials in Czechia

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Genetic Diseases, Inborn Status: Completed Country / region: Czechia Clear all

6 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20091
20131
20181
20191
20221

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed6

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
NewAmsterdam Pharma1
Novo Nordisk A/S1
PTC Therapeutics1
Pfizer1
Swedish Orphan Biovitrum1
Vertex Pharmaceuticals Incorporated1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Genetic Diseases, Inborn6
Blood Coagulation Disorders1
Coagulation Protein Disorders1
Cystic Fibrosis1
Dermatitis1
Dermatitis, Atopic1
Dwarfism, Pituitary1
Dyslipidemias1
Eczema1
Fibrosis1

Trials

Showing 1 to 6 of 6. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.