Clinical trials
Phase 2 Genetic Diseases, Inborn trials in France
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
14 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2010 | 2 |
| 2011 | 3 |
| 2018 | 1 |
| 2019 | 2 |
| 2020 | 1 |
| 2021 | 2 |
| 2026 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 7 |
| Terminated | 3 |
| Enrolling by invitation | 2 |
| Recruiting | 2 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Novartis Pharmaceuticals | 3 |
| QED Therapeutics, a BridgeBio company | 3 |
| Alnylam Pharmaceuticals | 1 |
| Assistance Publique - Hôpitaux de Paris | 1 |
| CSL Behring | 1 |
| GenSight Biologics | 1 |
| Intergroupe Francophone du Myelome | 1 |
| Laboratoires Thea | 1 |
| Novo Nordisk A/S | 1 |
| Pharnext S.C.A. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 14 |
| Bone Diseases | 3 |
| Fragile X Syndrome | 3 |
| Mucopolysaccharidosis IV | 3 |
| Musculoskeletal Diseases | 3 |
| Osteochondrodysplasias | 3 |
| Achondroplasia | 2 |
| Dwarfism | 2 |
| Eye Diseases | 2 |
| Hyperoxaluria, Primary | 2 |
Trials
Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.