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Clinical trials

Recruiting Genetic Diseases, Inborn trials in France

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Genetic Diseases, Inborn Status: Recruiting Country / region: France Clear all

20 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20151
20212
20223
20231
20244
20254
20265

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting20

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
ModernaTX, Inc.3
Assistance Publique - Hôpitaux de Paris2
Hospices Civils de Lyon2
Imagine Institute2
Institut National de la Santé Et de la Recherche Médicale, France2
Assistance Publique Hopitaux De Marseille1
Avidity Biosciences, Inc.1
CSL Behring1
Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts1
Friedreich's Ataxia Research Alliance1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Genetic Diseases, Inborn20
Nervous System Diseases5
Autoimmune Diseases3
Metabolism, Inborn Errors3
Rare Diseases3
Acid-Base Imbalance2
Acidosis2
Amino Acid Metabolism, Inborn Errors2
Immune System Diseases2
Metabolic Diseases2

Trials

Showing 1 to 20 of 20. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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