Clinical trials
Observational Genetic Diseases, Inborn trials in Germany
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
20 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2006 | 1 |
| 2008 | 1 |
| 2010 | 1 |
| 2015 | 2 |
| 2017 | 3 |
| 2018 | 2 |
| 2019 | 1 |
| 2022 | 1 |
| 2023 | 4 |
| 2024 | 1 |
| 2025 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 10 |
| Recruiting | 4 |
| Withdrawn | 2 |
| Enrolling by invitation | 1 |
| Active, not recruiting | 1 |
| Terminated | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Novo Nordisk A/S | 3 |
| CENTOGENE GmbH Rostock | 2 |
| University of Bonn | 2 |
| Azafaros B.V. | 1 |
| BioMarin Pharmaceutical | 1 |
| CSL Behring | 1 |
| Charite University, Berlin, Germany | 1 |
| Editas Medicine, Inc. | 1 |
| Friedreich's Ataxia Research Alliance | 1 |
| Imagine Institute | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 20 |
| Lysosomal Storage Diseases | 5 |
| Lipid Metabolism Disorders | 3 |
| Metabolic Diseases | 3 |
| Metabolism, Inborn Errors | 3 |
| Nervous System Diseases | 3 |
| Rare Diseases | 3 |
| Blood Coagulation Disorders | 2 |
| Bone Diseases, Metabolic | 2 |
| Brain Diseases | 2 |
Trials
Showing 1 to 20 of 20. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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