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Clinical trials

Terminated Genetic Diseases, Inborn trials in Germany

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Genetic Diseases, Inborn Status: Terminated Country / region: Germany Clear all

6 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20112
20141
20151
20161
20181

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Terminated6

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Novartis Pharmaceuticals2
Dicerna Pharmaceuticals, Inc., a Novo Nordisk company1
PTC Therapeutics1
Quince Therapeutics S.p.A.1
Shire1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Genetic Diseases, Inborn6
Fragile X Syndrome2
Metabolic Diseases2
Nervous System Diseases2
Ataxia Telangiectasia1
Brain Diseases1
Brain Diseases, Metabolic, Inborn1
Central Nervous System Diseases1
Demyelinating Diseases1
Genetic Diseases, X-Linked1

Trials

Showing 1 to 6 of 6. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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