Clinical trials
Recruiting Genetic Diseases, Inborn trials in Italy
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
15 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2015 | 1 |
| 2017 | 1 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 3 |
| 2024 | 1 |
| 2025 | 3 |
| 2026 | 4 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 15 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| IRCCS Eugenio Medea | 2 |
| Avidity Biosciences, Inc. | 1 |
| BioMarin Pharmaceutical | 1 |
| CSL Behring | 1 |
| Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta | 1 |
| Fondazione Policlinico Universitario Agostino Gemelli IRCCS | 1 |
| Fondazione SISA (Societa Italiana per lo Studio della Arteriosclerosi) | 1 |
| Friedreich's Ataxia Research Alliance | 1 |
| IRCCS Azienda Ospedaliero-Universitaria di Bologna | 1 |
| Imagine Institute | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 15 |
| Rare Diseases | 4 |
| Musculoskeletal Diseases | 3 |
| Nervous System Diseases | 3 |
| Anemia, Sickle Cell | 2 |
| Bone Diseases | 2 |
| Neuromuscular Diseases | 2 |
| Achondroplasia | 1 |
| Adrenoleukodystrophy | 1 |
| Alexander Disease | 1 |
Trials
Showing 1 to 15 of 15. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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