Skip to content

Clinical trials

Phase 1/2 Genetic Diseases, Inborn trials in the Netherlands

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Genetic Diseases, Inborn Phase: Phase 1/2 Country / region: Netherlands Clear all

7 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20161
20213
20222
20241

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting3
Active, not recruiting2
Terminated2

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
ModernaTX, Inc.5
REGENXBIO Inc.1
Vertex Pharmaceuticals Incorporated1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Genetic Diseases, Inborn7
Metabolism, Inborn Errors4
Metabolic Diseases3
Acid-Base Imbalance2
Acidosis2
Amino Acid Metabolism, Inborn Errors2
Propionic Acidemia2
Atherosclerosis1
Cardiovascular Diseases1
Glucose Metabolism Disorders1

Trials

Showing 1 to 7 of 7. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.