Clinical trials
Completed Genetic Diseases, Inborn trials in the Netherlands
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
21 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2004 | 2 |
| 2006 | 2 |
| 2009 | 3 |
| 2010 | 1 |
| 2011 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2017 | 1 |
| 2018 | 2 |
| 2019 | 3 |
| 2022 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 21 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Pharming Technologies B.V. | 4 |
| Novo Nordisk A/S | 3 |
| Alexion Pharmaceuticals, Inc. | 1 |
| Alnylam Pharmaceuticals | 1 |
| Editas Medicine, Inc. | 1 |
| Erasmus Medical Center | 1 |
| Kastle Therapeutics, LLC | 1 |
| Leiden University Medical Center | 1 |
| NewAmsterdam Pharma | 1 |
| Novartis Pharmaceuticals | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 21 |
| Metabolic Diseases | 4 |
| Congenital Abnormalities | 3 |
| Infant, Newborn, Diseases | 3 |
| Lipid Metabolism Disorders | 3 |
| Lipid Metabolism, Inborn Errors | 3 |
| Metabolism, Inborn Errors | 3 |
| Angioedemas, Hereditary | 2 |
| Cystic Fibrosis | 2 |
| Digestive System Diseases | 2 |
Trials
Showing 1 to 21 of 21. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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