Clinical trials
Recruiting Genetic Diseases, Inborn trials in Portugal
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
3 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2024 | 1 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 3 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| AIRNA Corporation | 1 |
| Grifols Therapeutics LLC | 1 |
| QED Therapeutics, a BridgeBio company | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 3 |
| Emphysema | 2 |
| Lung Diseases | 2 |
| Pathologic Processes | 2 |
| Respiratory Tract Diseases | 2 |
| Subcutaneous Emphysema | 2 |
| alpha 1-Antitrypsin Deficiency | 2 |
| Bone Diseases | 1 |
| Congenital Abnormalities | 1 |
| Dwarfism | 1 |
Trials
Showing 1 to 3 of 3. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.