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Clinical trials

Recruiting Genetic Diseases, Inborn trials in Spain

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Genetic Diseases, Inborn Status: Recruiting Country / region: Spain Clear all

12 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20131
20161
20213
20221
20231
20241
20251
20263

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Recruiting12

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
ModernaTX, Inc.3
Asociación Española para el Estudio del Hígado2
AIRNA Corporation1
Avidity Biosciences, Inc.1
Friedreich's Ataxia Research Alliance1
Grifols Therapeutics LLC1
Imagine Institute1
Institut Investigacio Sanitaria Pere Virgili1
QED Therapeutics, a BridgeBio company1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Genetic Diseases, Inborn12
Metabolism, Inborn Errors3
Acid-Base Imbalance2
Acidosis2
Amino Acid Metabolism, Inborn Errors2
Emphysema2
Infant, Newborn, Diseases2
Lung Diseases2
Metabolic Diseases2
Musculoskeletal Diseases2

Trials

Showing 1 to 12 of 12. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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