Clinical trials
Phase 1 Genetic Diseases, Inborn trials in the United Kingdom
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
3 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2009 | 1 |
| 2023 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 2 |
| Recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| AIRNA Corporation | 1 |
| AlgiPharma AS | 1 |
| PepGen Inc | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 3 |
| Lung Diseases | 2 |
| Respiratory Tract Diseases | 2 |
| Congenital Abnormalities | 1 |
| Cystic Fibrosis | 1 |
| Digestive System Diseases | 1 |
| Emphysema | 1 |
| Heredodegenerative Disorders, Nervous System | 1 |
| Infant, Newborn, Diseases | 1 |
| Liver Diseases | 1 |
Trials
Showing 1 to 3 of 3. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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