Clinical trials
Phase 4 Genetic Diseases, Inborn trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
3 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2016 | 1 |
| 2020 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 2 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Maimonides Medical Center | 1 |
| University of California, Davis | 1 |
| University of Pennsylvania | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 3 |
| Chromosome Disorders | 2 |
| Intellectual Disability | 2 |
| Neurobehavioral Manifestations | 2 |
| Abnormalities, Multiple | 1 |
| Congenital Abnormalities | 1 |
| Diabetes Mellitus, Type 2 | 1 |
| Excoriation Disorder | 1 |
| Fragile X Syndrome | 1 |
| Genetic Diseases, X-Linked | 1 |
Trials
Showing 1 to 3 of 3. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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