Skip to content

Clinical trials

Active, not recruiting Genetic Diseases, Inborn trials with no applicable phase

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Genetic Diseases, Inborn Phase: Not applicable Status: Active, not recruiting Clear all

9 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20201
20211
20223
20231
20241
20252

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Active, not recruiting9

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Grand Valley State University2
Vanderbilt University Medical Center2
Abramson Cancer Center at Penn Medicine1
Brigham and Women's Hospital1
Massachusetts General Hospital1
Mayo Clinic1
Michigan State University1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Genetic Diseases, Inborn9
Cerebral Palsy2
Spinal Cord Injuries2
Spinal Dysraphism2
Cardiovascular Diseases1
Genetic Predisposition to Disease1
Learning Disabilities1
Motor Skills Disorders1
Muscular Atrophy, Spinal1
Neoplasms1

Trials

Showing 1 to 9 of 9. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.