Clinical trials
Not yet recruiting Genetic Diseases, Inborn trials with no applicable phase
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
5 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2024 | 1 |
| 2025 | 1 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Not yet recruiting | 5 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Assistance Publique - Hôpitaux de Paris | 1 |
| Genethon | 1 |
| Hospices Civils de Lyon | 1 |
| Unity Health Toronto | 1 |
| metaX Institut fuer Diatetik GmbH | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 5 |
| Amino Acid Metabolism, Inborn Errors | 1 |
| Ataxia | 1 |
| Brain Diseases | 1 |
| Brain Diseases, Metabolic | 1 |
| Brain Diseases, Metabolic, Inborn | 1 |
| Central Nervous System Diseases | 1 |
| Cerebellar Ataxia | 1 |
| Metabolic Diseases | 1 |
| Metabolism, Inborn Errors | 1 |
Trials
Showing 1 to 5 of 5. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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