Clinical trials
Recruiting Genetic Diseases, Inborn trials with no applicable phase
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
21 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2016 | 1 |
| 2020 | 1 |
| 2022 | 2 |
| 2024 | 9 |
| 2025 | 6 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 21 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Hospices Civils de Lyon | 2 |
| IRCCS Eugenio Medea | 2 |
| Murdoch Childrens Research Institute | 2 |
| Rady Pediatric Genomics & Systems Medicine Institute | 2 |
| Fondazione Policlinico Universitario Agostino Gemelli IRCCS | 1 |
| Lipidica, a.s. | 1 |
| Masaryk Memorial Cancer Institute | 1 |
| National Cancer Institute (NCI) | 1 |
| Professor Ernest Hung-Yu Ng | 1 |
| Rigshospitalet, Denmark | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 21 |
| Rare Diseases | 3 |
| Communication Disorders | 2 |
| Pancreatitis, Chronic | 2 |
| Adrenoleukodystrophy | 1 |
| Amino Acid Metabolism, Inborn Errors | 1 |
| Aneuploidy | 1 |
| Apraxias | 1 |
| Autoimmune Diseases | 1 |
| Brain Diseases | 1 |
Trials
Showing 1 to 21 of 21. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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