Clinical trials
Genetic Diseases, Inborn trials with no applicable phase and unknown status
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
10 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2016 | 2 |
| 2017 | 1 |
| 2019 | 2 |
| 2021 | 1 |
| 2023 | 2 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Unknown status | 10 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Assistance Publique - Hôpitaux de Paris | 1 |
| Boston Children's Hospital | 1 |
| Fairview University Medical Center | 1 |
| Istanbul University | 1 |
| Menarini Biomarkers Singapore | 1 |
| Meyer Children's Hospital IRCCS | 1 |
| Rady Pediatric Genomics & Systems Medicine Institute | 1 |
| Shaare Zedek Medical Center | 1 |
| The University of Queensland | 1 |
| University of Leicester | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 10 |
| Immune System Diseases | 2 |
| Primary Immunodeficiency Diseases | 2 |
| Aortic Diseases | 1 |
| Aortic Dissection | 1 |
| Ataxia | 1 |
| Ataxia Telangiectasia | 1 |
| Brain Diseases | 1 |
| Cardiovascular Diseases | 1 |
| Central Nervous System Diseases | 1 |
Trials
Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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