Clinical trials
Completed Phase 2/3 Genetic Diseases, Inborn trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
4 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2004 | 1 |
| 2009 | 1 |
| 2015 | 1 |
| 2018 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 4 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Pharming Technologies B.V. | 1 |
| Radboud University Medical Center | 1 |
| University of Washington, the Collaborative Health Studies Coordinating Center | 1 |
| Vertex Pharmaceuticals Incorporated | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 4 |
| Digestive System Diseases | 2 |
| Adenoma | 1 |
| Adenomatous Polyposis Coli | 1 |
| Adenomatous Polyps | 1 |
| Cystic Fibrosis | 1 |
| Digestive System Neoplasms | 1 |
| Duodenal Neoplasms | 1 |
| Gastrointestinal Diseases | 1 |
| Gastrointestinal Neoplasms | 1 |
Trials
Showing 1 to 4 of 4. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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