Clinical trials
Phase 2 Genetic Diseases, Inborn trials with unknown status
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
6 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2011 | 1 |
| 2012 | 1 |
| 2016 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Unknown status | 6 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Center for Research Resources (NCRR) | 2 |
| General Hospital of Chinese Armed Police Forces | 1 |
| Imperial College London | 1 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 1 |
| Protalix | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 6 |
| Rare Diseases | 3 |
| Cystic Fibrosis | 2 |
| Respiratory Tract Diseases | 2 |
| Brain Neoplasms | 1 |
| Cerebellar Ataxia | 1 |
| Cholestasis | 1 |
| Digestive System Diseases | 1 |
| Disease | 1 |
| Gastrointestinal Diseases | 1 |
Trials
Showing 1 to 6 of 6. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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