Clinical trials
Completed Phase 4 Genetic Diseases, Inborn trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
6 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2010 | 1 |
| 2016 | 1 |
| 2020 | 1 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 6 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Novo Nordisk A/S | 3 |
| Hospital Ruber Internacional | 1 |
| Maimonides Medical Center | 1 |
| University of California, Davis | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genetic Diseases, Inborn | 6 |
| Turner Syndrome | 3 |
| Chromosome Disorders | 2 |
| Intellectual Disability | 2 |
| Nervous System Diseases | 2 |
| Neurobehavioral Manifestations | 2 |
| Abnormalities, Multiple | 1 |
| Brain Diseases | 1 |
| Congenital Abnormalities | 1 |
| Drug Resistant Epilepsy | 1 |
Trials
Showing 1 to 6 of 6. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.